Drug Development Pipeline
Restore CFTR Function
PTI-801 is a new CFTR corrector. Correctors are drugs designed to fix and restore the function of the defective CFTR protein. The corrected CFTR then moves to the cell surface, where it functions as a chloride channel and helps maintain the right balance of fluid in the airways.
A phase 1 & 2 study to test the safety and tolerability of PTI-801 is underway.
This program is sponsored by Proteostasis Therapeutics. It is being conducted through the Therapeutics Development Network.
Sign up for clinical trial alerts
Get email updates about clinical trials that matter to you.
Explore clinical trials
Be a part of the movement transforming the future of cystic fibrosis treatment.Learn More