Revised Law Includes Designated Funding for Rare Diseases
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New Patient Data Posted Online Shows Improvements Across Care Center Network
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Historic Time in Treatment of Rare Disease as Promising Drugs Reach Phase 3 Trials
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Legislation to Help Speed Research for Cystic Fibrosis and Other Rare Diseases
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Cystic Fibrosis Foundation Drug Development Model Spawns More Than 30 Promising Therapies
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