Historic Time in Treatment of Rare Disease as Promising Drugs Reach Phase 3 Trials
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Legislation to Help Speed Research for Cystic Fibrosis and Other Rare Diseases
Bill Would Remove Financial Penalties for Participating in Research Studies
Learning that your baby has cystic fibrosis may come as a shock, especially if you do not have a family history of the disease, but you are not alone.
CFF-Championed Bill Eliminates Barriers to Participation in Clinical Trials for People with CF and other Rare Diseases
Today, the Cystic Fibrosis Foundation announced a new award of up to $2 million to Eloxx Pharmaceuticals Inc. to support the global Phase 2 clinical program of ELX-02, a potential therapy to treat people with cystic fibrosis who have nonsense mutations.
The Cystic Fibrosis Foundation is awarding up to $15.9 million in additional funding to Eloxx Pharmaceuticals Inc. to expand clinical studies of ELX-02, a potential therapy for people with CF who have nonsense mutations.
Study reaffirms the Foundation’s commitment to advance solutions to the growing challenge of antibiotic resistance
Observational study supported by the CF Foundation will monitor real-world experience with Trikafta