Cystic Fibrosis Foundation Therapeutics (CFFT) and industry are tackling this disease from every angle. During the next two months, we will be sharing video updates from leaders in the field talking about the different approaches that CFFT is taking to help support its drug development pipeline to address the major aspects of the disease.
Dr. Drucy Borowitz explains why fixing the CFTR protein is important to people living with CF and talks about the development of several small molecule drugs that target many of the different types of CFTR mutations.
Dr. Manu Jain shares more about the three approaches that researchers are using that could take us closer than ever to a cure. These new approaches include everything from gene editing, to therapies that correct RNA, to new drugs that target the defective CFTR protein. These new drugs and technologies are being studied in the lab and in early-phase clinical trials.