Promising Data For CF Drug Published in The Lancet
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Positive data for PTC124, one of the first potential therapies to address the basic defect in CF were published today in The Lancet. The Phase 2 data show that treatment with PTC124 improves the function of the faulty CFTR protein in patients with a specific type of CF mutation known as nonsense-mutation. The Lancet is one of the oldest peer-reviewed medical journals in the world.

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About the CF Foundation | CFTR Modulators | Genetic Therapies
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