Proteostasis will continue to focus its research and development on small molecules that correct defective
In the Delta F508 mutation, the defective
In addition to this collaboration, CFFT is investing in a robust pipeline of potential therapies that target CF from every angle, including research collaborations with Pfizer, Genzyme and Vertex to accelerate the discovery and development of new drugs.
CFFT's and the Foundation's goal is to find effective therapies and a cure for 100 percent of people with the disease.
Proteostasis Therapeutics develops disease-modifying therapeutics for orphan and neurodegenerative diseases.
- Explore other CF therapies in development in our interactive pipeline.