Legislation Would Increase Patient and Expert Participation in FDA Review of Rare Disease Treatments
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CFF-Championed Bill Eliminates Barriers to Participation in Clinical Trials for People with CF and other Rare Diseases
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Legislation Includes Measures to Increase Patient and Expert Participation in FDA Review of Rare Disease Drugs
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Senate Caucus will work with House Caucus to raise awareness, advance policies and support research
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