Revised Law Includes Designated Funding for Rare Diseases
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Cystic Fibrosis Foundation Drug Development Model Spawns More Than 30 Promising Therapies
Today, the Cystic Fibrosis Foundation announced a new award of up to $2 million to Eloxx Pharmaceuticals Inc. to support the global Phase 2 clinical program of ELX-02, a potential therapy to treat people with cystic fibrosis who have nonsense mutations.
Legislation would leave millions with inadequate, unaffordable care as they battle chronic and other major health conditions.
Today, the Cystic Fibrosis Foundation announced that it has awarded up to $400,000 to Life Edit Therapeutics Inc. to explore the application of their unique gene editing technology in CF.
Patient and provider groups urge the Senate to work together in a bipartisan fashion to ensure that Americans have access to affordable health care.