Historic Time in Treatment of Rare Disease as Promising Drugs Reach Phase 3 Trials
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Legislation to Help Speed Research for Cystic Fibrosis and Other Rare Diseases
Foundation and Legislative Supporters Pushed for Bill
Bill Would Remove Financial Penalties for Participating in Research Studies
Kids from 20 States Make Case for Drug Funding and Access to Care for Fatal Disease
CFF-Championed Bill Eliminates Barriers to Participation in Clinical Trials for People with CF and other Rare Diseases
Today, the Cystic Fibrosis Foundation announced a new award of up to $2 million to Eloxx Pharmaceuticals Inc. to support the global Phase 2 clinical program of ELX-02, a potential therapy to treat people with cystic fibrosis who have nonsense mutations.
Un diagnóstico de fibrosis quística no debe descalificar a una persona para recibir atención que pueda salvarle la vida.