Cystic fibrosis is caused by mutations in the gene responsible for producing the cystic fibrosis transmembrane conductance regulator (CFTR) protein. For this reason, scientists are exploring ways to provide a correct copy of the gene to treat CF.
Site Search
Cystic fibrosis is caused by mutations in both copies of the cystic fibrosis transmembrane conductance regulator (CFTR) gene. Scientists are examining whether it is possible to correct the mutations through a process called gene editing.
For
Clinical trials are critical to developing new treatments for CF. So, how exactly does an experimental drug become an approved therapy?
There have never been more opportunities to help develop new drugs for cystic fibrosis than there are today. When you are deciding whether to participate in a
When participating in a clinical trial, nothing is more important than your safety. We go the extra mile when it comes to protecting study volunteers.
Learn how your child's
Theratyping matches therapies, or medications, to specific types of mutations. The primary goal of theratyping is to identify which mutations respond to certain CFTR modulators, thereby helping people with rare CFTR mutations gain access to already approved modulators quickly and safely.
The Cystic Fibrosis Foundation is requesting letters of intent for research projects that aim to identify biomarkers, improve knowledge of pathogenesis, and explore new approaches to treatment of chronic lung allograft dysfunction (CLAD).
When you are deciding whether to join a clinical trial, you should consider logistics.