Here's what you need to know about the four CFTR (cystic fibrosis transmembrane conductance regulator) modulators.
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Las siguientes preguntas y respuestas abordan inquietudes de la comunidad sobre el COVID-19 y la escuela.
Drugs that target the underlying defect in the cystic fibrosis transmembrane conductance regulator (
Encuentra respuestas a preguntas sobre la pandemia del COVID-19 mientras vives con fibrosis quística.
Because of the COVID-19 outbreak, millions of Americans, including those living with cystic fibrosis and their families, are facing tough decisions around employment. The issue of paid leave and its eligibility is emerging as a top concern for people with CF and working members of their family.
Estamos buscando tratamientos potenciales para las personas con FQ que tienen mutaciones raras y sin sentido. Es posible que no aprovechen de los moduladores, que corrigen la proteína reguladora de la conductancia transmembrana de la fibrosis quística (CFTR, por sus siglas en inglés) que funciona mal.
Find answers to questions about the COVID-19 pandemic while living with cystic fibrosis.
Theratyping matches therapies, or medications, to specific types of mutations. The primary goal of theratyping is to identify which mutations respond to certain CFTR modulators, thereby helping people with rare CFTR mutations gain access to already approved modulators quickly and safely.